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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
CD38
Becker BMD muscular dystrophy
Clinical trials
L-Type
CaVβs
Myotendinous junction
Molecular Sequence Data
Animal/physiopathology
LKB1
Centronuclear myopathy
Myogenesis
Mdx mouse
Morphogenesis
Gene expression
Cell Line
Gene Expression Regulation/drug effects
Hear
Antisense oligonucleotides
MES
Cardiomyopathy
Metabolism
Becker muscular dystrophy
Long QT
Muscle Strength
Muscle Biology
Animals
Dystrophine
Mitochondrial fission
NNOS
CaV subunits
LncARN
Exon skipping
Allele‐specific silencing therapy
Cachexia
Muscle
DMO
Multiresolution modeling
Dystrophie Musculaire de Becker BMD
Long noncoding RNA
Base Sequence
Muscular dystrophy
Duchenne DMD dystrophy
Hepatocellular carcinoma
Immunoglobulin Fc Fragments/pharmacology
Muscular Dystrophy
Dynamin 2
Inbred C57BL
Muscles/physiopathology
Calcium Channels
Invivo
Male
Muscle development
Genomic
Duchenne muscular dystrophy DMD
Dystrophy
Dystrophie Musculaire de Duchenne DMD
Liver
Energy Metabolism/drug effects
Activin Receptors
DMD
Drp1
Epigenetics
Dystrophie musculaire de Becker
Mice
Inhibitors
Multi resolution modeling
Muscular Atrophy
Modificateurs de gènes
Dystrophin-EGFP
Cell homeostasis
Homeostasis
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Dystrophin
Cells
Multi exon skipping
Humans
NAD+
Cultured
Dystrophin central domain
Autophagy
LncRNA
Calcium
Diseases
Cell Biology
Ex-vivo
Gene modifiers
DHPR α1S
BMD
Skeletal muscle
CTNNB1
Génomique
Knockout
Molecular docking
MiARN
Duchenne muscular dystrophy
Becker muscular dystrophy BMD
Inbred mdx
Human Umbilical Vein Endothelial Cells
Delivery
Cardiomyopathie