Loading...
Derniers dépôts
Nombre de documents
Nombre de notices
widget_cloud
Spinal muscular atrophy
Inflammation
FSHD
Myopathy
DMD
Cell therapy
Errance diagnostique
RNA biology
CTG repeat contractions
Brain
LMNA gene
Congenital myopathy
Mouse model
Therapy
Alternative splicing
COVID-19
Duchenne muscular dystrophy
Neuromuscular diseases
PABPN1
Thymus
ALS
Aging
Rare diseases
Glutamate
Lamin A/C
Actin
Laminopathie
Cardiomyopathy
Long read sequencing
Gene therapy
Regeneration
Transcriptomics
Skeletal muscle
Fabry disease
Autoimmunity
Muscle
Autoantibodies
Antisense oligonucleotides
Myotonic Dystrophy type 1
Laminopathies
Heart failure
Lamin A/C LMNA gene
Autophagy
Exercise
Dynamin 2
Becker muscular dystrophy
Biomarkers
Mechanotransduction
Cytoskeleton
Myositis
Thérapie génique
Autoimmune diseases
Rare neuromuscular diseases
Biomarker
Myogenesis
Satellite cell
Myotonic Dystrophy
Calcium
Satellite cells
OPMD
Dermatomyositis
AAV
Neuromuscular disease
Humans
Fibrosis
Mice
Cytokines
Dilated cardiomyopathy
Myotonic dystrophy
Aged
Laminopathy
Nuclear envelope
Cancer
Male
MBNL
Myasthenia Gravis MG
RNA interference
Motoneuron
Amyotrophic lateral sclerosis
CMS
Outcome measures
Dystrophin
Genotype phenotype correlation
Muscle regeneration
Neuromuscular junction
Treatment
Muscular dystrophy
Myopathies
CRISPRi
Animals
Myoblasts
Trinucleotide repeat expansion
Congenital muscular dystrophy
Transgenic mouse model
Myasthenia gravis
Centronuclear myopathy
LMNA
Heart
Myotonic dystrophy type 1
Astrocyte